MTE #5: Gene-Based Therapy in Liver Disease—Promise, Ethics, and Responsibilities (Ticketed)

About this session

Gene therapy trials for liver diseases present unprecedented opportunities for both patients and investigators. While offering the potential for durable disease modification for patients, gene therapies also raise complex questions for investigators regarding informed consent, heightened safety monitoring requirements, equity of access, pediatric enrollment, long-term follow-up obligations, and investigator responsibility for therapies with potentially irreversible effects.

Speakers

• LD

  Lorenzo D'Antiga

  Hospital Papa Giovanni XXIII, Bergamo.

  Facilitator

• JT

  Jeffery Teckman

  saint louis university school of medicine

  Facilitator